Harnessing Bayesian Methods: Tackling Challenges in Rare Disease and Small Population Trials

1 minute read

Published: May 27th, 2025

Sponsors working in rare diseases/running small population studies often have difficulties in demonstrating efficacy due to the small number of patients available for analyses. Bayesian methods offer promising solutions for small population and rare disease trials where leveraging available data can provide important insights and evidence. Discover the importance of Bayesian trial designs and the different ways and situations that they can be utilized.

This webinar is part of our three-part online series. To book a place on the final session of this series, click here.

Speakers:

  • Giles Partington, Consultant Statistician
  • Moderator: Christina Geyer, Principal Statistician

Learning Points:

  • Understand Bayesian methods – key differentiators from standard methodologies usually seen by regulators.
  • How to use Bayesian methodologies in rare diseases and small population trials to provide valuable insights.
  • Explore a case study where Bayesian methods were implemented in a rare disease setting.


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